AAV1 Mediated Co-expression of Formylglycine-Generating Enzyme and Arylsulfatase A Efficiently Corrects Sulfatide Storage in a Mouse Model of Metachromatic Leukodystrophy
| Autor: | Kurai, Toshiyuki, Hisayasu, Sanae, Kitagawa, Ryo, Migita, Makoto, Suzuki, Hidenori, Hirai, Yukihiko, Shimada, Takashi |
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| Zdroj: | In Molecular Therapy January 2007 15(1):38-43 |
| Databáze: | ScienceDirect |
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