AAV1.NT-3 Gene Therapy for Charcot–Marie–Tooth Neuropathy

Autor: Sahenk, Zarife, Galloway, Gloria, Clark, Kelly Reed, Malik, Vinod, Rodino-Klapac, Louise R, Kaspar, Brian K., Chen, Lei, Braganza, Cilwyn, Montgomery, Chrystal, Mendell, Jerry R
Zdroj: In Molecular Therapy March 2014 22(3):511-521
Databáze: ScienceDirect