Sleeping Beauty Transposon Vectors in Liver-directed Gene Delivery of LDLR and VLDLR for Gene Therapy of Familial Hypercholesterolemia

Autor: Turunen, Tytteli A K, Kurkipuro, Jere, Heikura, Tommi, Vuorio, Taina, Hytönen, Elisa, Izsvák, Zsuzsanna, Ylä-Herttuala, Seppo
Zdroj: In Molecular Therapy March 2016 24(3):620-635
Databáze: ScienceDirect