Hematopoietic Stem Cell Gene Therapy for the Multisystemic Lysosomal Storage Disorder Cystinosis
| Autor: | Harrison, Frank, Yeagy, Brian A, Rocca, Celine J, Kohn, Donald B, Salomon, Daniel R, Cherqui, Stephanie |
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| Zdroj: | In Molecular Therapy February 2013 21(2):433-444 |
| Databáze: | ScienceDirect |
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