Broad Functional Correction of Molecular Impairments by Systemic Delivery of scAAVrh74-hSGSH Gene Delivery in MPS IIIA Mice
| Autor: | Duncan, F Jason, Naughton, Bartholomew J, Zaraspe, Kimberly, Murrey, Darren A, Meadows, Aaron S, Clark, Kelly Reed, Newsom, David E, White, Peter, Fu, Haiyan, McCarty, Douglas M |
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| Zdroj: | In Molecular Therapy April 2015 23(4):638-647 |
| Databáze: | ScienceDirect |
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