Fully Deleted Adenovirus Persistently Expressing GAA Accomplishes Long-Term Skeletal Muscle Glycogen Correction in Tolerant and Nontolerant GSD-II Mice

Autor: Kiang, Anne, Hartman, Zachary C., Liao, Shaoxi, Xu, Fang, Serra, Delila, Palmer, Donna J., Ng, Philip, Amalfitano, Andrea
Zdroj: In Molecular Therapy January 2006 13(1):127-134
Databáze: ScienceDirect