Correction of metabolic, craniofacial, and neurologic abnormalities in MPS I mice treated at birth with adeno-associated virus vector transducing the human α-l-iduronidase gene
| Autor: | Hartung, Seth D, Frandsen, Joel L, Pan, Dao, Koniar, Brenda L, Graupman, Patrick, Gunther, Roland, Low, Walter C, Whitley, Chester B, McIvor, R.Scott * |
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| Zdroj: | In Molecular Therapy June 2004 9(6):866-875 |
| Databáze: | ScienceDirect |
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