Base editor-mediated correction of a BTK Mutation in XLA Patient Hematopoietic Stem Cells restores Human B cell development

Autor: Zea-Vera, Andres, Bzhilyanskaya, Vera, Dahl, Gary, Meis, Ron, Kleinstiver, Ben, Bergerson, Jenna, Malech, Harry, De ravin, Suk See
Zdroj: In Clinical Immunology May 2023 250 Supplement
Databáze: ScienceDirect