Intracerebral gene therapy in children with mucopolysaccharidosis type IIIB syndrome: an uncontrolled phase 1/2 clinical trial
| Autor: | Tardieu, Marc, Zérah, Michel, Gougeon, Marie-Lise, Ausseil, Jérome, de Bournonville, Stéphanie, Husson, Béatrice, Zafeiriou, Dimitrios, Parenti, Giancarlo, Bourget, Philippe, Poirier, Béatrice, Furlan, Valérie, Artaud, Cécile, Baugnon, Thomas, Roujeau, Thomas, Crystal, Ronald G, Meyer, Christian, Deiva, Kumaran, Heard, Jean-Michel |
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| Zdroj: | In The Lancet Neurology September 2017 16(9):712-720 |
| Databáze: | ScienceDirect |
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