An antisense oligonucleotide against SOD1 delivered intrathecally for patients with SOD1 familial amyotrophic lateral sclerosis: a phase 1, randomised, first-in-man study
| Autor: | Miller, Timothy M, Pestronk, Alan, David, William, Rothstein, Jeffrey, Simpson, Ericka, Appel, Stanley H, Andres, Patricia L, Mahoney, Katy, Allred, Peggy, Alexander, Katie, Ostrow, Lyle W, Schoenfeld, David, Macklin, Eric A, Norris, Daniel A, Manousakis, Georgios, Crisp, Matthew, Smith, Richard, Bennett, C Frank, Bishop, Kathie M, Cudkowicz, Merit E |
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| Zdroj: | In Lancet Neurology May 2013 12(5):435-442 |
| Databáze: | ScienceDirect |
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