DEVELOPMENT OF A GMP MANUFACTURING PROCESS FOR BASE EDITED HEMATOPOIETIC STEM AND PROGENITOR CELLS (BE-HSPCS) FOR X-LINKED CHRONIC GRANULOMATOUS DISEASE (X-CGD)
Autor: | Lei, H., Jin, J., Ma, M., Cai, Y., Jin, P., Stroncek, D., Malech, H., De Ravin, S., Highfill, S.L. |
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Zdroj: | In Cytotherapy June 2024 26(6) Supplement:S28-S29 |
Databáze: | ScienceDirect |
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