DEVELOPMENT OF A GMP MANUFACTURING PROCESS FOR BASE EDITED HEMATOPOIETIC STEM AND PROGENITOR CELLS (BE-HSPCS) FOR X-LINKED CHRONIC GRANULOMATOUS DISEASE (X-CGD)

Autor: Lei, H., Jin, J., Ma, M., Cai, Y., Jin, P., Stroncek, D., Malech, H., De Ravin, S., Highfill, S.L.
Zdroj: In Cytotherapy June 2024 26(6) Supplement:S28-S29
Databáze: ScienceDirect