Successful immune tolerance induction to enzyme replacement therapy in CRIM-negative infantile Pompe disease

Autor: Messinger, Yoav H., Mendelsohn, Nancy J., Rhead, William, Dimmock, David, Hershkovitz, Eli, Champion, Michael, Jones, Simon A., Olson, Rebecca, White, Amy, Wells, Cara, Bali, Deeksha, Case, Laura E., Young, Sarah P., Rosenberg, Amy S., Kishnani, Priya S.
Zdroj: In Genetics in Medicine January 2012 14(1):135-142
Databáze: ScienceDirect