Approaches to the Assessment of Clinical Benefit of Treatments for Conditions That Have Heterogeneous Symptoms and Impacts: Potential Applications in Rare Disease

Autor: Murray, Lindsey T., Howell, Timothy A., Matza, Louis S., Eremenco, Sonya, Adams, Heather R., Trundell, Dylan, Coons, Stephen Joel
Zdroj: In Value in Health April 2023 26(4):547-553
Databáze: ScienceDirect