Home infusion experience in patients with Pompe disease receiving avalglucosidase alfa during three clinical trials

Autor: Díaz-Manera, Jordi a, ⁎, Hughes, Derralynn b, Erdem-Özdamar, Sevim c, Tard, Céline d, Béhin, Anthony e, Bouhour, Françoise f, Davison, James g, m, Hahn, Si Houn h, Haack, Kristina An i, Huynh-Ba, Olivier i, Periquet, Magali j, 1, Tammireddy, Swathi k, Thibault, Nathan k, Zhou, Tianyue k, van der Ploeg, Ans T. l
Zdroj: In Molecular Genetics and Metabolism December 2024 143(4)
Databáze: ScienceDirect