Pompe disease: Unmet needs and emerging therapies

Autor: George, Kelly A., Anding, Allyson L., van der Flier, Arjan, Tomassy, Giulio S., Berger, Kenneth I., Zhang, Tracy Y., Sardi, S. Pablo
Zdroj: In Molecular Genetics and Metabolism November 2024 143(3)
Databáze: ScienceDirect