Community consensus for Heparan sulfate as a biomarker to support accelerated approval in Neuronopathic Mucopolysaccharidoses

Autor: Muenzer, Joseph, Ho, Carole, Lau, Heather, Dant, Mark, Fuller, Maria, Boulos, Nidal, Dickson, Patricia, Ellinwood, N. Matthew, Jones, Simon A., Zanelli, Eric, O'Neill, Cara
Zdroj: In Molecular Genetics and Metabolism August 2024 142(4)
Databáze: ScienceDirect