Breaking the chains of lipoprotein lipase deficiency: A pediatric perspective on the efficacy and safety of Volanesorsen

Autor: den Hollander, Bibiche, Brands, Marion M., Nijhuis, Ilse J.M., Doude van Troostwijk, Lous J.A.E., van Essen, Peter, Hofsteenge, Geesje H., Koot, Bart G., Müller, Annelieke R., Tseng, Laura A., Stroes, Erik S.G., van de Ven, Peter M., Wiegman, Albert, van Karnebeek, Clara D.M.
Zdroj: In Molecular Genetics and Metabolism May 2024 142(1)
Databáze: ScienceDirect