Long-term comparative effectiveness of pegvaliase versus medical nutrition therapy with and without sapropterin in adults with phenylketonuria
| Autor: | Burton, Barbara K., Clague, Gillian E., Harding, Cary O., Kucuksayrac, Ece, Levy, Drew G., Lindstrom, Kristin, Longo, Nicola, Maillot, François, Muntau, Ania C., Rutsch, Frank, Zori, Roberto T. |
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| Zdroj: | In Molecular Genetics and Metabolism January 2024 141(1) |
| Databáze: | ScienceDirect |
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