Anti-human-TfR-GAA efficiently clears CNS and muscle glycogen in a translatable hTfR-KI/Pompe disease mouse model
| Autor: | van der Flier, Arjan, Riley, Raquel, Smith, Laurie, Kinton, Sofia, Zhou, Shan, Kistanova, Elena, Bodinizzo, Renee, Guo, Lilu, Maloney, Colleen, Morel, Caroline, Bangari, Dinesh S., Haack, Kristina An, George, Kelly |
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| Zdroj: | In Molecular Genetics and Metabolism February 2024 141(2) |
| Databáze: | ScienceDirect |
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