Cerliponase alfa for the treatment of CLN2 disease in a patient cohort including children under 3 years of age
| Autor: | Schulz, Angela, de los Reyes, Emily C., Specchio, Nicola, Gissen, Paul, Slasor, Peter, Bondade, Shailesh, Cohen Pfeffer, Jessica L. |
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| Zdroj: | In Molecular Genetics and Metabolism February 2024 141(2) |
| Databáze: | ScienceDirect |
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