AAV-ARSA mediated gene replacement for the treatment of metachromatic leukodystrophy
| Autor: | Ramachandran, Shyam, Ardinger, Jeffery, Ramos, MiAngela, Guo, Lilu, Hossain, Mahmud, Ayloo, Swathi, Adams, Johanna, McCarty, William, Nass, Shelley, Goulet, Martin, Mueller, Christian |
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| Zdroj: | In Molecular Genetics and Metabolism February 2024 141(2) |
| Databáze: | ScienceDirect |
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