A long-term observation of ophthalmology assessment in atypical CLN2 patients receiving ICV cerliponase alfa treatment
| Autor: | Kao, Audrey, Chang, Harriet, Bhola, Rahul, Wang, Raymond Y. |
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| Zdroj: | In Molecular Genetics and Metabolism February 2024 141(2) |
| Databáze: | ScienceDirect |
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