Therapeutic potential of intracerebroventricular recombinant human heparan-N-sulfatase enzyme replacement therapy in MPS IIIA mice

Autor: Jin, Dongkyu, Yang, Aram, Ko, Ah-ra, Yu, Yeongju, Uhm, Hyeong Seok, Jo, Inyoung, Kim, Sujeong, Kim, SoRa, Kim, Minju
Zdroj: In Molecular Genetics and Metabolism February 2024 141(2)
Databáze: ScienceDirect