Characteristics and management of US pediatric patients with Gaucher disease from the Gaucher Outcome Survey

Autor: Goker-Alpan, Ozlem, Burrow, Andrew, Enns, Gregory M., Ficicioglu, Can, Kishnani, Priya S., Ortiz, Damara, Prada, Carlos E., Vats, Divya, Weinreb, Neal J., Robinson, Ian, Pathak, Ravi R., Wright, Ekaterina, Botha, Jaco, Wilcox, William R.
Zdroj: In Molecular Genetics and Metabolism February 2024 141(2)
Databáze: ScienceDirect