A phase 2, randomized, double-blind, placebo-controlled, multicentre study to evaluate the efficacy and safety of pentosan polysulfate sodium in treating subjects with mucopolysaccharidosis VI: Study update
| Autor: | Giugliani, Roberto, Gravance, Curtis, Krishnan, Ravi, Eldon, Michael, Imperiale, Michael |
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| Zdroj: | In Molecular Genetics and Metabolism February 2024 141(2) |
| Databáze: | ScienceDirect |
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