Intracerebroventricular enzyme replacement therapy in patients with neuronopathic mucopolysaccharidosis type II: Final report of 5-year results from a Japanese open-label phase 1/2 study
| Autor: | Seo, Joo-Hyun, Kosuga, Motomichi, Hamazaki, Takashi, Shintaku, Haruo, Okuyama, Torayuki |
|---|---|
| Zdroj: | In Molecular Genetics and Metabolism December 2023 140(4) |
| Databáze: | ScienceDirect |
| Externí odkaz: |
|
Full Text from ScienceDirect