Patient reported outcomes of patients with Gaucher disease type 1 treated with eliglustat in real-world settings: The ELIPRO study

Autor: Camou, Fabrice, Lagadec, Audrey, Coutinho, Angela, Berger, Marc G., Cador-Rousseau, Bérengère, Gaches, Francis, Belmatoug, Nadia
Zdroj: In Molecular Genetics and Metabolism November 2023 140(3)
Databáze: ScienceDirect