Differences in organ abundance of iduronate 2-sulfatase and intravenous recombinant enzyme delivery: Potential implications for clinical response to ERT in MPS II
| Autor: | Shamoun, Alex J., Madrid, Kyle, Ferreira, Leonardo, Labilloy, Anatalia |
|---|---|
| Zdroj: | In Molecular Genetics and Metabolism February 2023 138(2) |
| Databáze: | ScienceDirect |
| Externí odkaz: |
|
Full Text from ScienceDirect