STAAR, a phase I/II study of isaralgagene civaparvovec (ST-920) gene therapy in adults with Fabry disease: Dose escalation phase results
| Autor: | Hopkin, Robert J., Ganesh, Jaya, Deegan, Patrick, Goker-Alpan, Ozlem, Bernat, John, Wilcox, William R., Pahl, Madeleine V., Whitley, Chester B., Hughes, Derralynn, Nicholls, Kathleen, Cao, Liching, Chen, Michael, Shiue, Lisa H., Bowden, Emma, Jaggumantri, Sravan, Passalacqua, Cristobal, Souberbielle, Bernard, Cockroft, Bettina M. |
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| Zdroj: | In Molecular Genetics and Metabolism February 2023 138(2) |
| Databáze: | ScienceDirect |
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