AAV-mediated gene therapy for galactosialidosis: A long-term safety and efficacy study
| Autor: | Fremuth, Leigh E., Hu, Huimin, van de Vlekkert, Diantha, Weesner, Jason A., Gomero, Elida M., d'Azzo, Alessandra |
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| Zdroj: | In Molecular Genetics and Metabolism February 2023 138(2) |
| Databáze: | ScienceDirect |
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