Twice weekly dosing with sebelipase alfa rescues severely ill infants with Wolman disease

Autor: Lopez, Maria Jose De Castro, de Frutos, Laura López, Brammeier, Kathryn L., Church, Heather J., Couce, Maria Luz, Jones, Simon, Ghosh, Arunabha
Zdroj: In Molecular Genetics and Metabolism February 2023 138(2)
Databáze: ScienceDirect