eP256 - HST5040: An investigational oral small molecule therapy entering phase 2 clinical development for methylmalonic (MMA) and propionic (PA) acidemias

Autor: Cox, Gerald, Armstrong, Allison, Waller, Mavis, Hayes, Mark, Collado, Maria Sol, Henke, Brad, Summar, Marshall, Wamhoff, Brian, Reardon, John, Figler, Robert, Johns, Brian, Chapman, Kimberly
Zdroj: In Molecular Genetics and Metabolism April 2021 132 Supplement 1:S162-S162
Databáze: ScienceDirect