PR001 gene therapy increased GCase activity and improved Gaucher disease type 1 phenotypes in mouse models
| Autor: | Sheehan, Patty, Heckman, Laura D., Wong, Li Chin, Yang, Zhaohui, Lin, Hsuan-Ni, Kamalakaran, Sid, Garimalla, Swetha, Politi, Jason, Dai, Yong, Hefti, Franz, Abeliovich, Asa |
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| Zdroj: | In Molecular Genetics and Metabolism February 2021 132(2):S100-S100 |
| Databáze: | ScienceDirect |
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