The GuardOne clinical trial: A first-in-human, open-label, multinational phase 1/2 study of AVR-RD-02 ex vivo lentiviral vector, autologous gene therapy for Gaucher disease
| Autor: | Jacobsen, Leslie, Kerner, Julie A., Ciotti, Rachel, Golipour, Azadeh, Yang, Josie, Pfeifer, Richard, Khan, Aneal, Mason, Chris |
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| Zdroj: | In Molecular Genetics and Metabolism February 2021 132(2):S51-S52 |
| Databáze: | ScienceDirect |
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