Long-term efficacy and safety of migalastat treatment in Fabry disease: 30-month results from the open-label extension of the randomized, phase 3 ATTRACT study

Autor: Feldt-Rasmussen, Ulla, Hughes, Derralynn, Sunder-Plassmann, Gere, Shankar, Suma, Nedd, Khan, Olivotto, Iacopo, Ortiz, Damara, Ohashi, Toya, Hamazaki, Takashi, Skuban, Nina, Yu, Julie, Barth, Jay A., Nicholls, Kathleen
Zdroj: In Molecular Genetics and Metabolism September-October 2020 131(1-2):219-228
Databáze: ScienceDirect
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