Pegvaliase for the treatment of phenylketonuria: Results of the phase 2 dose-finding studies with long-term follow-up

Autor: Burton, Barbara K., Longo, Nicola, Vockley, Jerry, Grange, Dorothy K., Harding, Cary O., Decker, Celeste, Li, Mingjin, Lau, Kelly, Rosen, Orli, Larimore, Kevin, Thomas, Janet
Zdroj: In Molecular Genetics and Metabolism August 2020 130(4):239-246
Databáze: ScienceDirect