AVR-RD-01 lentiviral gene therapy reduces Gb3 substrate in endothelial cells of renal peritubular capillaries in a previously untreated classic Fabry disease male patient
| Autor: | Volck, Birgitte, Fallet, Shari, Thomas, Mark, Carnley, Benedict, Golipour, Azadeh, Phillips, Dawn, Mason, Chris |
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| Zdroj: | In Molecular Genetics and Metabolism February 2020 129(2):S156-S157 |
| Databáze: | ScienceDirect |
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