Baseline patient characteristics of followME, a new, patient-centric, prospective, observational Fabry disease registry that evaluates migalastat, ERT, and a natural history cohort

Autor: Sunder-Plassmann, Gere, Bichet, Daniel G., Davidonis, Martynas, Germain, Dominique P., Giugliani, Roberto, Hopkin, Robert J., Jovanovic, Ana, Linhart, Ales, Nicholls, Kathleen, Nordbeck, Peter, Feldt-Rasmussen, Ulla, Rutecki, Jasmine, Giuliano, Joe, Skuban, Nina, Krusinska, Eva, Politei, Juan
Zdroj: In Molecular Genetics and Metabolism February 2020 129(2):S150-S150
Databáze: ScienceDirect
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