Intra-articular AAV9 α-iduronidase gene therapy in mucopolysaccharidosis type I canine model

Autor: Kan, Shih-hsin, Zhang, Haoyue, Smith, Jodi D., Snella, Elizabeth M., Afshin, Aminian, Jens, Jackie K., Valentine, Bethann, Dickson, Patricia I., Ellinwood, N. Matthew, Young, Sarah, Wang, Raymond Y.
Zdroj: In Molecular Genetics and Metabolism February 2020 129(2):S82-S83
Databáze: ScienceDirect