Design of a prospective, multicenter, multinational, observational safety and outcomes registry in Fabry disease patients treated with migalastat and untreated patients

Autor: Sunder-Plassmann, Gere, Bichet, Daniel G., Davidonis, Martynas, Germain, Dominique P., Giugliani, Roberto, Hopkin, Robert, Jovanovic, Ana, Linhart, Ales, Nicholls, Kathleen, Nordbeck, Peter, Feldt-Rasmussen, Ulla, Rutecki, Jasmine, Giuliano, Joe, Skuban, Nina, Politei, Juan
Zdroj: In Molecular Genetics and Metabolism February 2019 126(2):S140-S141
Databáze: ScienceDirect