The pro-inflammatory immunophenotype of a Farber disease mouse model is ameliorated by repeated dosing with RVT-801, a developmental enzyme replacement therapy for Farber disease

Autor: Sampey, Brante P., Duke, Katie S., Sampey, Gavin C., Gaukel, Eric J., Solyom, Alexander, Wring, Stephen A., He, Xingxuan, Zhu, Changzhi, DeAngelis, Victor, Schuchman, Edward H., Coquery, Christine M.
Zdroj: In Molecular Genetics and Metabolism February 2019 126(2):S128-S128
Databáze: ScienceDirect