Low-dose agalsidase beta treatment in male pediatric patients with Fabry disease: A 5-year randomized controlled trial

Autor: Ramaswami, Uma, Bichet, Daniel G., Clarke, Lorne A., Dostalova, Gabriela, Fainboim, Alejandro, Fellgiebel, Andreas, Forcelini, Cassiano M., An Haack, Kristina, Hopkin, Robert J., Mauer, Michael, Najafian, Behzad, Scott, C. Ronald, Shankar, Suma P., Thurberg, Beth L., Tøndel, Camilla, Tylki-Szymanska, Anna, Bénichou, Bernard, Wijburg, Frits A.
Zdroj: In Molecular Genetics and Metabolism May 2019 127(1):86-94
Databáze: ScienceDirect
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