Renal outcomes with up to 9 years of migalastat in patients with Fabry disease: Results from an open-label extension study

Autor: Nicholls, Kathleen, Giugliani, Roberto, Schiffmann, Raphael, Hughes, Derralynn A., Jain, Vipul, Holdbrook, Fred, Skuban, Nina, Castelli, Jeffery P., Barth, Jay A.
Zdroj: In Molecular Genetics and Metabolism February 2018 123(2):S105-S106
Databáze: ScienceDirect