Agreement between the results of meta-analyses from case reports and from clinical studies regarding the efficacy of laronidase therapy in patients with mucopolysaccharidosis type I who initiated enzyme replacement therapy in adult age: An example of case reports meta-analyses as an useful tool for evidence-based medicine in rare diseases

Autor: Sampayo-Cordero, Miguel a, ⁎, Miguel-Huguet, Bernat b, Pardo-Mateos, Almudena c, Moltó-Abad, Marc a, Muñoz-Delgado, Cecilia d, Pérez-López, Jordi a
Zdroj: In Molecular Genetics and Metabolism February 2018 123(2):69-75
Databáze: ScienceDirect
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