UX007 for the treatment of long chain-fatty acid oxidation disorders: Safety and efficacy in children and adults following 24 weeks of treatment
| Autor: | Vockley, J., Burton, B., Berry, G.T., Longo, N., Phillips, J., Sanchez-Valle, A., Tanpaiboon, P., Grunewald, S., Murphy, E., Humphrey, R., Mayhew, J., Bowden, A., Zhang, L., Cataldo, J., Marsden, D.L., Kakkis, E. |
|---|---|
| Zdroj: | In Molecular Genetics and Metabolism April 2017 120(4):370-377 |
| Databáze: | ScienceDirect |
| Externí odkaz: |
|
Full Text from ScienceDirect