Long-term results of ENGAGE: a phase 3, randomized, double‑blind, placebo-controlled, multi‑center study investigating the efficacy and safety of eliglustat in adults with type 1 Gaucher disease
| Autor: | Mistry, Pramod K, Lukina, Elena, Turkia, Hadhami Ben, Shankar, Suma, Feldman, Hagit Baris, Ghosn, Marwan, Mehta, Atul, Packman, Seymour, Lau, Heather, Petakov, Milan, Assouline, Sarit, Balwani, Manisha, Danda, Sumita, Hadjiev, Evgueniy, Ortega, Andres, Wu, Yaoshi, Gaemers, Sebastiaan J.M., Judith Peterschmitt, M. |
|---|---|
| Zdroj: | In Molecular Genetics and Metabolism January-February 2017 120(1-2):S97-S98 |
| Databáze: | ScienceDirect |
| Externí odkaz: |
|
Full Text from ScienceDirect