Liver-based expression of the human alpha-galactosidase A gene (GLA) in a murine Fabry model results in continuous supra-physiological enzyme activity and effective substrate reduction
| Autor: | Huston, Marshall W., Yasuda, Makiko, Pagant, Silvere, St. Martin, Susan, Sproul, Scott, Santiago, Yolanda, DeKelver, Russel, Holmes, Michael C., Desnick, Robert, Wechsler, Thomas |
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| Zdroj: | In Molecular Genetics and Metabolism January-February 2017 120(1-2):S69-S69 |
| Databáze: | ScienceDirect |
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