Elosulfase alfa treatment and changes in physical functioning and disability in Morquio syndrome type A

Autor: Hendriksz, Christian J., Parini, Rossella, AlSayed, Moeenaldeen D., Raiman, Julian, Giugliani, Roberto, Mitchell, John J., Burton, Barbara K., Guelbert, Norberto, Stewart, Fiona, Hughes, Derralynn A., Matousek, Robert, Hawley, Sara M., Decker, Celeste, Harmatz, Paul R.
Zdroj: In Molecular Genetics and Metabolism January-February 2017 120(1-2):S65-S65
Databáze: ScienceDirect