GAA deficiency in Pompe disease is alleviated by exon inclusion in iPS cell-derived skeletal muscle cells
| Autor: | Bergsma, Atze J, van der Wal, Erik, Pijnenburg, Joon M., van Gestel, Tom J.M., in 't Groen, Stijn L.M., Zaehres, Holm, Araúzo-Bravo, Marcos J., Schöler, Hans R., van der Ploeg, Ans T., Pim Pijnappel, W.W.M. |
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| Zdroj: | In Molecular Genetics and Metabolism January-February 2017 120(1-2):S27-S27 |
| Databáze: | ScienceDirect |
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