Long-term hematological, visceral, and growth outcomes in children with Gaucher disease type 3 treated with imiglucerase in the International Collaborative Gaucher Group Gaucher Registry
| Autor: | El-Beshlawy, Amal, Tylki-Szymanska, Anna, Vellodi, Ashok, Belmatoug, Nadia, Grabowski, Gregory A., Kolodny, Edwin H., Batista, Julie L., Cox, Gerald F., Mistry, Pramod K. |
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| Zdroj: | In Molecular Genetics and Metabolism January-February 2017 120(1-2):47-56 |
| Databáze: | ScienceDirect |
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